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US Patent Number

9,567,585

Publication Date

2-14-2017

Abstract

The present invention provides, among other things, oligonucleotide modulators of human 5'-HT2C receptor (HTR2C) and improved methods and composition for treating HTR2C-related diseases, disorders or conditions based on such modulators. In particular, oligonucleotides modulators according to the invention target specific regions in the Exon V/Intron V junction of the human HTR2C pre-mRNA and drive expression of HTR2C Vb splice isoform, leading to increased generation of non-edited strong HTR2C receptor and enhanced serotonin receptor activity.

Assignees

Shire Human Genetic Therapies, Inc., Lexington, MA (US); University of Kentucky, Lexington, KY (US)

Application Number

14/357,388

Filing Date

11-9-2012

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